The NF-κB signaling pathway plays a pivotal role in how our bodies fight infection, heal, and regulate inflammation. At the ...

The FDA approved pegcetacoplan (Empaveli; Apellis Pharmaceuticals) as the first treatment for patients 12 years and older with the rare, severe kidney diseases C3 glomerulopathy (C3G) and primary ...

Ayodeji Adegunsoye, MD, PhD, MSc, highlights how the underrepresentation of minority populations in pulmonary fibrosis genetic studies hinders accurate disease risk prediction and broader clinical ...

Prince Frederik of Luxembourg, the youngest son of Prince Robert of Luxembourg and Princess Julie of Nassau, passed away at ...

Princess Charlotte proved she is becoming the biggest sports fan in the royal family as she joined Prince William to see England win the Euro 2025 final in Switzerland July 27.

The Revell family hoped a gene therapy could buy time for their sons, who have a rare and fatal disease. After two patients ...

OpEd: The Trump administration’s deep cuts to medical research at universities and the NIH ensures that those suffering with ...

Over a year after King Charles III revealed his cancer diagnosis, he gave a simple explanation of how he is feeling as he ...

The Purdy family shares their insights on navigating their child’s rare neurodegenerative disease and their direct ...

“It is trying to treat a devastating lifelong disease by fixing it at its source. We are able to fix the actual genetic problem to significantly benefit and improve these people’s lives rathe… ...

AscellaHealth’s Patient-Focused Approach is Best-in-Class Model for Distribution of Rare Disease Therapies Provided by GlobeNewswire Jul 15, 2025, 7:00:00 AM ...

Shares of rare-earth stock USA Rare Earth are climbing today despite the absence of news from the company. A newly announced partnership between MP Materials and Apple is likely partly responsible ...