Understanding human gene function in living organisms has long been hampered by fundamental differences between species.

Scientists first read the human genome, a three-billion-letter biological book, in April 2003. Since then, researchers have steadily advanced the ability to write DNA, moving far beyond single-gene ...

CRISPR–Cas9-based therapies are widely investigated for their clinical applications. However, there are limitations ...

Understanding human gene function in living organisms has long been hampered by fundamental differences between species. Although mice share most ...

The clearance allows human trials for its one-time treatment targeting a genetic eye disease that causes vision loss.

He Jiankui spent three years in prison after creating gene-edited babies. Now back at work, he sees a greater opening for ...

A stretch of viral DNA in the mouse genome gives cells in early-stage embryos the potential to become almost any cell type in ...

Machine learning models reveal that histone marks are predictive of gene expression across human cell types and highlight important nuances between natural control and the effects of CRISPR-Cas9-based ...

New name reflects the Company’s strategic evolution focused on later-stage preclinical assets leveraging its most advanced, signature ...

Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...