Around 25 million Americans have a rare genetic disease, and many of them struggle with not only a lack of effective ...

Common ancestor eels lost the aquaporin gene encoding proteins with broad solute permeability. Researchers from the Institute ...

The same pulling force that causes “tears” in a glass of wine also shapes embryos. It’s another example of how genes exploit ...

Iain Cheeseman and colleagues reveal the underappreciated role of single genes producing multiple proteins in atypical ...

Scientists discover a new gene therapy technique that may reverse ALS by restoring vital RNA signals, providing hope for ...

Translation factors eIF1A and eIF5B are key repressors of an abnormal protein translation process linked to neurodegenerative ...

In a world-first trial, scientists used a one-off CRISPR gene edit to switch off a liver “fat brake” gene, slashing stubborn ...

Although the genetic cause of many diseases have been identified, it's estimated that as many as 70% of patients with a rare ...

Although heart cells and skin cells contain identical instructions for creating proteins encoded in their DNA, they're able ...

Transition Bio and Voyager have teamed to discover and develop new small molecules that target toxic TDP-43 protein clumps in ...

NEW ORLEANS – A single injection of a gene-edited protein was deemed productive and safe in patients with dyslipidemia that ...