After a meeting with the FDA, Scholar Rock is planning a 2026 resubmission of its application seeking approval of apitegromab ...

Like one of her favorite poems describes, columnist Brianna Albers always feels like she's digging herself out of a new hole in her life.

Zolgensma outperformed Spinraza in achieving a more sustained clinical response for children with SMA type 1, a comparative ...

Combining the experimental and approved SMA therapies BIO101 and Spinraza in the lab was found to improve muscle function in ...

Family caregivers express immense devotion to others, but they should also remember self-care, writes columnist.

Spinraza (nusinersen) may help stabilize lung function in people with SMA types 2 and 3, delaying the need for breathing ...

Most children SMA type 1 can survive an episode of pARDS, a life-threatening respiratory failure, under standard protocols, ...

For columnist Alyssa Silva, control has always been her safety net. But in reality, it doesn't protect her; it exhausts her.

When columnist Connie Chandler tackles an art project, it becomes a creative collaboration thanks to her supportive team of ...

Try these practical tips for travel with SMA, with advice on packing, accessible accommodations, and health management.

A study found mutations that cause SMA may trigger problems with bone cell communication, suggesting a potential new way to treat weak bones.