Leaders with CureDuchenne say approvals are expected this year for several new treatments for Duchenne MD, making it "an ...

All muscular dystrophies cause muscle weakness, but life expectancy can vary dramatically between types of muscular dystrophy.

An international team of scientists has designed a new type of therapy to target the mutant toxic RNA that causes myotonic ...

What is strength? Columnist Patrick Moeschen believes it's the act of persevering through events that are beyond our control.

The U.S. Food and Drug Administration has awarded orphan drug status to Atossa Therapeutics' (Z)-endoxifen for Duchenne ...

Navigating Duchenne muscular dystrophy (DMD) is a journey with challenges at every stage. From recognizing early signs to managing daily life, understanding genetics and heart health is key. With the ...

In boys with DMD, executive skills such as self-control begin to lag around age 8, but show signs of partial catch-up by 14, ...

With a progressive disease like FSHD, the loss of abilities and independence has an unpredictable timeline, says columnist.

January doesn’t just bring a new calendar year. For four of us in this family, it’s when we celebrate our birthdays. A new year of life! I live in Nebraska with my husband and six of the seven ...

My family and I are part of a community of boys, men, and families living with Duchenne muscular dystrophy. That community extends far beyond the U.S., where we live. Families uniquely experience ...