At age 45, Dr. Lakiea Bailey said, for the longest time, that she was the oldest person with sickle cell anemia that she knew. The executive director of the nonprofit patient advocacy group the Sickle ...

FILE - This July 2019 image provided by the Sarah Cannon Research Institute shows Victoria Gray on her infusion day during a gene editing trial for sickle cell disease at the Sarah Cannon Research ...

Gene and cell therapies bring fresh hope to people with genetic disorders, but recovery can be complex and long-term support remains sparse. For most of her life, Genesis Jones’s daily routine ...

Nearly a year after its approval, the first medical treatment that uses the Nobel Prize–winning technology Crispr is now being given to patients. Called Casgevy, the gene-editing treatment is for ...

The Food and Drug Administration on Friday approved a new gene-editing therapy to treat sickle cell disease, a debilitating blood disorder that affects at least 100,000 Americans, most of whom are ...

For the first time in 20 years, a new therapy for sickle cell disease is to be made available on the NHS. Crizanlizumab (Adakveo) has been recommended by The National Institute for Health and Care ...

Incredible new data presented recently at the European Hematology Association Congress has revealed an experimental CRISPR gene editing therapy is both safe and effective up to three years after ...

SAN DIEGO — A newly approved gene therapy product for sickle cell disease, lovotibeglogene autotemcel (lovo-cel, marketed as Lyfgenia), led to durable disease remissions for up to 5 years and almost ...

Heather Avant always dresses up when she goes to the emergency room. “I’ve been conditioned to act and behave in a very specific way,” said Avant. “I try to do my hair. I make sure I shower, have nice ...

Most patients living with sickle cell disease who went to the emergency department of a U.S. hospital with a severe pain crisis were not triaged properly and faced long delays. Those triaged with a ...